Information on the current research on Duchenne Myscular Dystrophy


001 gene therapy
Date Name of File Contributor
14-06-30 Gene therapy in Duchenne muscular dystrophy Peter B. Kang
14-01-09 Utrophin Upregulation - Duchenne Muscular Distrophy Annemieke Aartsma-Rus
14-01-08 Gene Therapy Duchenne Muscular Distrophy patients Annemieke Aartsma-Rus
14-01-06 Correction of the dystrophin gene Jacques P. Tremblay


002 cell therapies
Date Name of File Contributor
14-05-27 TRANSPLANTATION OF DONOR MESOANGIOBLASTS FOR DUCHENNE MUSCULAR DYSTROPHY A PHASE I/IIa CLINICAL TRIAL Giulio Cossu
14-05-06 Dr. Rita Perlingeiro Research - Pluripotent Steam Cells and Duchenne Muscular Distrophy Rita Perlingeiro
14-01-08 Cell Therapy - Duchenne Muscular Distrophy Annemieke Aartsma-Rus
14-01-07 Stem cell therapy for Duchenne Muscular Dystrophy Jacques P. Tremblay
14-01-06 Myoblast transplantation for Duchenne Muscular Dystrophy Jacques P. Tremblay
13-12-16 ROLE OF CD133+ STEM CELLS IN FUTURE CLINICAL PERSPECTIVES FOR DMD PATIENTS Dr. YVAN TORRENTE - Lay summary YVAN TORRENTE


003 exon skipping
Date Name of File Contributor
14-02-03 Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping Lauren Hache, Andrea Smith
14-02-03 Becker Muscular Dystrophy- A Natural History Study to Predict Efficacy of Exon Skipping Laura Hache, Andrea Smith, Lisa Hunegs
14-01-29 Duchenne Muscular Distrophy Dr Takeda Shinichi Takeda
14-01-08 Exon Skipping Duchenne Muscular Distrophy Annemieke Aartsma-Rus


004 Heat Shock protein
Date Name of File Contributor


005 Halofuginone
Date Name of File Contributor
14-01-09 Halufoginone - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


006 IGF-1
Date Name of File Contributor


007 laminin-111
Date Name of File Contributor


008 myostatin inhibition
Date Name of File Contributor
14-01-09 Myostatin Inhibition - Increasing Muscle Mass or Quality - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


009 surgical treatment of DMD
Date Name of File Contributor


010 osteopontin
Date Name of File Contributor


011 exercise for DMD
Date Name of File Contributor
14-05-23 Distrophy Muscular Distrophy Report Exercises Silvia Gianola Silvia Gianola
14-02-03 A multicenter collaborative study on the clinical features, expression profiling, and quality of life of infantile onset facioscapulohumeral muscular dystrophy Zoë Sund and Lauren Hache
14-02-03 Longitudinal Study of the Relationship between Impairment, Activity Limitation, Participation and Quality of Life in Persons with Confirmed Duchenne Muscular Dystrophy Zoë Sund and Lauren Hache


012 heart failure in DMD
Date Name of File Contributor


013 coenzyme Q
Date Name of File Contributor
14-02-03 PITT0908: Clinical Trial of CoenzymeQ10 and Lisinopril in Muscular Dystrophies Lauren Hache, Andrea Smith


014 spingosine-1-phosphate
Date Name of File Contributor


015 SERCA2a
Date Name of File Contributor


016 deflazacort
Date Name of File Contributor
14-01-08 Corticosteroids - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


017 utrophin
Date Name of File Contributor
14-03-26 Utrophin Modulation as a Disease Modifying Treatment for Duchenne muscular dystrophy (DMD) Kay Davies


018 ataluren
Date Name of File Contributor


019 idebenone
Date Name of File Contributor
14-01-08 Idebenone - Duchenne Muscular Distrophy Annemieke Aartsma-Rus
13-12-16 Idebenone (Catena®/Raxone®) as potential treatment option for Duchenne muscular dystrophy Gunnar Buyse


020 green tea EGCg
Date Name of File Contributor
14-01-09 Green Tea Extract - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


021 Aldosterone Antagonism
Date Name of File Contributor


022 Arbekacin sulfate
Date Name of File Contributor


023 Flavocoxid
Date Name of File Contributor


024 Sildenafil
Date Name of File Contributor
14-01-09 Revatio (Sildenafil) and Tadalafil - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


025 Nebivolol
Date Name of File Contributor


026 Ramipril
Date Name of File Contributor


027 - epicatechin
Date Name of File Contributor


028 CoenzymeQ10
Date Name of File Contributor


029 Givinostat
Date Name of File Contributor


030 L-arginine
Date Name of File Contributor


031 Drug Therapy
Date Name of File Contributor
14-01-08 Drug Therapy Duchenne Muscular Distrophy Patients Annemieke Aartsma-Rus


032 Ataluren, PTC124 and Gentamicin
Date Name of File Contributor
14-05-30 Ataluren new drug approved for DMD treatment Press
14-05-30 PTC124 and gentamicin for Duchenne Muscular Distrophy Annemieke Aartsma-Rus


033 Ciclosporine
Date Name of File Contributor
14-01-08 Ciclosporine - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


034 Follistatin Gene Delivery
Date Name of File Contributor
14-01-09 Follistatin Gene Delivery - Increasing Muscle Mass or Quality - Duchenne Muscular Distrophy Annemieke Aartsma-Rus


035 Telomeres and DMD
Date Name of File Contributor
14-05-06 A new mouse model for Duchenne Muscular Dystrophy developed in Dr. Blau laboratory Helen Blau



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